Rise for Rare is a bold three year $6 million campaign launched by To Cure A Rose Foundation to accelerate the development of genetic treatments for children with rare diseases. More than a fundraising initiative, Rise for Rare is a movement—uniting families, scientists, and advocates to disrupt a slow, fragmented system and build a faster, smarter path to cures.

We’re funding the science, the innovation, and the infrastructure needed to bring lifesaving therapies to life—not someday, but now. Because when the system says “too rare,” we rise and say: not rare to us.

We are Hope. A Path. A Way to a Cure.

We are Rise for Rare—built to give families more than a diagnosis. We give them a way forward.

Every dollar fuels urgent research in the lab, speeds therapies to children in need, and empowers families at the frontlines of rare disease. Together, we are building a future where no child is left behind because their condition was “too rare.”

Join the Movement

This is your moment to transform the future of rare disease treatment—for one child, for many, for generations to come.